| Efficient non-viral gene delivery into human hematopoietic stem cells by minicircle sleeping beauty transposon vectors M Holstein, C Mesa-Nuñez, C Miskey, E Almarza, V Poletti, M Schmeer, ... Molecular Therapy 26 (4), 1137-1153, 2018 | 69 | 2018 |
| In vivo imaging of lung inflammation with neutrophil-specific 68 Ga nano-radiotracer J Pellico, AV Lechuga-Vieco, E Almarza, A Hidalgo, C Mesa-Nuñez, ... Scientific reports 7 (1), 1-10, 2017 | 55 | 2017 |
| Lentiviral vector-mediated correction of a mouse model of leukocyte adhesion deficiency type I D Leon-Rico, M Aldea, R Sanchez-Baltasar, C Mesa-Nuñez, J Record, ... Human gene therapy 27 (9), 668-678, 2016 | 27 | 2016 |
| A phase 1/2 study of lentiviral-mediated ex-vivo gene therapy for pediatric patients with severe leukocyte adhesion deficiency-I (LAD-I): results from phase 1 DB Kohn, GR Rao, E Almarza, D Terrazas, E Nicoletti, A Fernandes, ... Blood 136, 15, 2020 | 9 | 2020 |
| A Phase 1/2 Study of Lentiviral-Mediated Ex-Vivo Gene Therapy for Pediatric Patients with Severe Leukocyte Adhesion Deficiency-I (LAD-I): Interim Results DB Kohn, G Rao, E Almarza, D Terrazas, E Nicoletti, A Fernandes, C Kuo, ... MOLECULAR THERAPY 29 (4), 19-20, 2021 | 4 | 2021 |
| A novel genetic variant in PTGS1 affects N‐glycosylation of cyclooxygenase‐1 causing a dominant‐negative effect on platelet function and bleeding diathesis V Palma‐Barqueros, M Crescente, ME de la Morena, MV Chan, ... American Journal of Hematology 96 (3), E83-E88, 2021 | 4 | 2021 |
| Gene Therapy for Lad-I Immunodeficiency: Preclinical Evaluation of HSC Transduction Under Optimized GMP-Conditions E Almarza, C Mesa-Nunez, C Damian, M Fernandez-Garcia, ... Blood 134, 5751, 2019 | 4 | 2019 |
| The downregulated membrane expression of CD18 in CD34+ cells defines a primitive population of human hematopoietic stem cells C Mesa-Núñez, D Leon-Rico, M Aldea, C Damián, R Sanchez-Baltasar, ... Stem cell research & therapy 11 (1), 1-9, 2020 | 3 | 2020 |
| ESGCT XXV Anniversary Congress in Collaboration with the German Society for Gene Therapy October 17–20, 2017 Berlin, Germany SM Maffioletti, S Sarcar, A Henderson, I Mannhardt, L Pinton, LA Moyle, ... Human Gene Therapy 28 (12), A1-A125, 2017 | 2 | 2017 |
| A novel genetic variant in PTGS1 affects N-glycosylation of cyclooxygenase-1 causing a dominant-negative effect. V Palma-Barqueros, M Crescente, ME de la Morena, MV Chan, E Almarza, ... American Journal of Hematology, 2020 | | 2020 |
| Lentiviral Vector-Mediated Gene Complementation for the Diagnosis of LAD-I C Mesa-Nunez, C Damian, K Gilmour, R Sanchez, O Alberquilla, ... MOLECULAR THERAPY 28 (4), 176-177, 2020 | | 2020 |
| A New Molecular Variant in the PTGS1 Gene That Abrogates Generation of Thromboxane A2 Synthesis and Associates with Platelet Dysfunction and Bleeding V Palma-Barqueros, M Chan, M Crescente, JM Bastida, E Almarza, ... Blood, The Journal of the American Society of Hematology 134 (Supplement_1 …, 2019 | | 2019 |
| Towards the lentiviral-mediated gene therapy for Glanzmann thrombasthenia V Palma-Barqueros, C Mesa-Nunez, C Damian, N Bohdan, U Modlich, ... HUMAN GENE THERAPY 30 (11), A81-A82, 2019 | | 2019 |
| Stable transduction of long-term HSCs under optimized GMP-conditions for the gene therapy of LAD-I patients C Mesa-Nunez, C Damian, M Fernandez-Garcia, B Diez-Cabezas, ... HUMAN GENE THERAPY 30 (11), A86-A87, 2019 | | 2019 |
| Preclinical model of gene therapy for leukocyte adhesion deficiency type I C Mesa Núñez | | 2019 |
| Gene Therapy of Patients with Leukocyte Adhesion Deficiency Type I (LAD-I): Preclinical Studies and Clinical Trial Design E Almarza, C Mesa-Nunez, C Damian, B Diez-Cabezas, ... MOLECULAR THERAPY 27 (4), 392-392, 2019 | | 2019 |
| Efficient and cost effective transduction of hematopoietic stem cells with lentiviral vectors for the treatment of leukocyte adhesion deficiency type I C Mesa-Nunez, C Damian, M Fernandez-Garcia, B Diez-Cabezas, ... HUMAN GENE THERAPY 29 (12), A39-A40, 2018 | | 2018 |
| Comprehensive preclinical studies for the gene therapy of patients with leukocyte adhesion deficiency type I (LAD-I) E Almarza, C Mesa-Nunez, C Damian, B Diez-Cabezas, ... HUMAN GENE THERAPY 29 (12), A28-A28, 2018 | | 2018 |
| Changing the Face of Modern Medicine: Stem Cell and Gene Therapy Organized Jointly by the European Society of Gene & Cell Therapy (ESGCT), International Society for Stem Cell … KM Champion, P Albertini, I Visigalli, F Cecere, N Carriglio, ... Human Gene Therapy 29 (12), A1-A169, 2018 | | 2018 |
| Preclinical Evaluation for the Gene Therapy of Patients with Leukocyte Adhesion Deficiency Type I E Almarza, C Mesa-Núñez, C Damián, M Fernández-García, ... Blood, The Journal of the American Society of Hematology 132 (Supplement 1 …, 2018 | | 2018 |
