| CRISPR-Cas9 gene editing of hematopoietic stem cells from patients with Friedreich’s ataxia CJ Rocca, JN Rainaldi, J Sharma, Y Shi, JH Haquang, J Luebeck, P Mali, ... Molecular Therapy Methods & Clinical Development 17, 1026-1036, 2020 | 26 | 2020 |
| Defining the activity of pro-reparative extracellular vesicles in wound healing based on miRNA payloads and cell type-specific lineage mapping DJ Park, W Choi, S Sayeed, RA Dorschner, J Rainaldi, K Ho, J Kezios, ... Molecular Therapy, 2024 | 1 | 2024 |
| Multimodal perturbation analyses of cyclin-dependent kinases reveal a network of synthetic lethalities associated with cell-cycle regulation and transcriptional regulation K Ford, BP Munson, SH Fong, R Panwala, WK Chu, J Rainaldi, ... Scientific reports 13 (1), 7678, 2023 | 1 | 2023 |
| Reprogramming Adeno-Associated Virus Tropism Via Displayed Peptides Tiling Receptor-Ligands A Portell, KM Ford, A Suhardjo, J Rainaldi, MN Bublik, M Sanghvi, ... bioRxiv, 2022.09. 26.509383, 2022 | | 2022 |
| Hematopoietic Stem Cell Gene Therapy For Mucopolysaccharidosis Type IIIC RA Badell-Grau, J Rainaldi, P Losay, K Doung, R Pithia, K Pakravesh, ... MOLECULAR THERAPY 30 (4), 300-301, 2022 | | 2022 |
| CRISPR-Cas9 Edited Hematopoietic Stem and Progenitor Cells for Friedreich's Ataxia A Sivakumar, JN Rainaldi, R Wan, CJ Rocca, S Cherqui MOLECULAR THERAPY 30 (4), 135-135, 2022 | | 2022 |
| Respect young scientists' time JN Rainaldi SCIENCE 376 (6588), 26-26, 2022 | | 2022 |
| Rules all PIs should follow JS Chen, CY Huang, S Lanke, MS Fernandopulle, Y Ji, Y Zhi, ... Science 376 (6588), 24-26, 2022 | | 2022 |
| Pandemic haiku Science 373 (6550), 22-23, 2021 | | 2021 |
| Modeling Friedreich's Ataxia with iPSC-Derived Brain Cells and Characterization of Neuronal Defects Due to FXN Deficiency P Mishra, JN Rainaldi, EA Hansen, J Nguyen, A Johnson, N Coufal, ... Molecular Therapy 29 (4), 277-277, 2021 | | 2021 |
| Transplantation of CRISPR/Cas9 Corrected Hematopoietic Stem and Progenitor Cells into a Mouse Model of Friedreich's Ataxia JN Rainaldi, CJ Rocca, MA Abreia, S Cherqui Molecular Therapy 29 (4), 266-267, 2021 | | 2021 |
| CRISPR/Cas9 Mediated Genetic Correction of Hematopoietic Stem Cells from Patients with Friedreich's Ataxia CJ Rocca, JN Rainaldi, J Sharma, S Yanmeng, JH Haquang, J Luebeck, ... Molecular Therapy 28 (4), 485-485, 2020 | | 2020 |
| Transplantation of Wild-Type Hematopoietic Stem and Progenitor Cells Improves Disease Phenotypes in Novel Mucopolysaccharidosis Iiic Mouse Model RA Badell-Grau, K Pakravesh, KE Thai, F Son, R Chen, J Rainaldi, ... | | |
