Therapeutic liver repopulation by transient acetaminophen selection of gene-modified hepatocytes A Vonada, A Tiyaboonchai, S Nygaard, J Posey, AM Peters, SR Winn, ... Science translational medicine 13 (597), eabg3047, 2021 | 20 | 2021 |
Self-cleaving guide RNAs enable pharmacological selection of precise gene editing events in vivo A Tiyaboonchai, A Vonada, J Posey, C Pelz, L Wakefield, M Grompe Nature communications 13 (1), 7391, 2022 | 5 | 2022 |
Complete correction of murine phenylketonuria by selection-enhanced hepatocyte transplantation A Vonada, L Wakefield, M Martinez, CO Harding, M Grompe, ... Hepatology 79 (5), 1088-1097, 2024 | 1 | 2024 |
Drug-Mediated Expansion of Transplanted Hepatocytes In Vivo A Vonada, A Tiyaboonchai, M Grompe MOLECULAR THERAPY 29 (4), 250-250, 2021 | 1 | 2021 |
Selective expansion of gene-targeted hepatocytes using acetaminophen leads to reproducible long-term liver repopulation A Vonada, S Nygaard, M Grompe MOLECULAR THERAPY 27 (4), 326-326, 2019 | 1 | 2019 |
In vivo tracing of the Cytokeratin 14 lineages using self-cleaving guide RNAs and CRISPR/Cas9 A Tiyaboonchai, L Wakefield, A Vonada, CL May, C Dorrell, D Enicks, ... Developmental Biology 504, 120-127, 2023 | | 2023 |
In Vivo Selection of Randomly Integrated rAAV Vectors A Tiyaboonchai, A Vonada, M Grompe MOLECULAR THERAPY 30 (4), 1-1, 2022 | | 2022 |
Correction of Phenylketonuria by Drug-Mediated Expansion of Transplanted Hepatocytes In Vivo A Vonada, A Tiyaboonchai, CO Harding, M Grompe MOLECULAR THERAPY 30 (4), 113-113, 2022 | | 2022 |
Selective Expansion of Gene-Targeted Hepatocytes In Vivo Leads to Therapeutic Levels of Transgene Expression A Vonada, S Nygaard, A Tiyaboonchai, J Posey, M Grompe MOLECULAR THERAPY 28 (4), 418-419, 2020 | | 2020 |
Self Cleaving Guide RNAs for Selective Expansion of Precisely Gene Edited Hepatocytes In Vivo A Tiyaboonchai, JA Posey, SC Nygaard, AG Vonada, M Grompe MOLECULAR THERAPY 27 (4), 70-70, 2019 | | 2019 |
Efficient In Vivo Selection of Gene-Targeted Hepatocytes Using Acetaminophen-Induced Liver Toxicity S Nygaard, A Vonada, M Grompe MOLECULAR THERAPY 26 (5), 431-431, 2018 | | 2018 |
Self Cleaving guideRNAs for Selective Expansion of Precisely Gene Edited Hepatocytes In Vivo A Tiyaboonchai, S Nygaard, A Vonada, M Grompe MOLECULAR THERAPY 26 (5), 228-228, 2018 | | 2018 |
Highly-Sensitive Quantification of Genome Editing Events Using Next Generation Amplicon Sequencing AG Vonada, SC Nygaard, M Grompe MOLECULAR THERAPY 26 (5), 363-364, 2018 | | 2018 |