Improved titer and gene transfer by lentiviral vectors using novel, small β-globin locus control region elements RA Morgan, MJ Unti, B Aleshe, D Brown, KS Osborne, C Koziol, ... Molecular Therapy 28 (1), 328-340, 2020 | 35 | 2020 |
Targeted cellular micropharmacies: cells engineered for localized drug delivery TJ Gardner, CM Bourne, MM Dacek, K Kurtz, M Malviya, L Peraro, ... Cancers 12 (8), 2175, 2020 | 21 | 2020 |
Creating new β-globin-expressing lentiviral vectors by high-resolution mapping of locus control region enhancer sequences RA Morgan, F Ma, MJ Unti, D Brown, PG Ayoub, C Tam, L Lathrop, ... Molecular therapy Methods & clinical development 17, 999-1013, 2020 | 13 | 2020 |
Highly efficient cellular expression of circular mRNA enables prolonged protein expression MJ Unti, SR Jaffrey Cell Chemical Biology 31 (1), 163-176. e5, 2024 | 2 | 2024 |
Creating New β-Globin-Expressing Lentiviral Vectors by High-Resolution Mapping of Locus RA Morgan, F Ma, MJ Unti | | 2020 |
beta-Globin Locus Control Region Core Sequences Driving Expression of Anti-Sickling Globin Ameliorates Disease Phenotype in a Mouse Model of Sickle Cell Disease RA Morgan, M Unti, RP Hollis, DB Kohn MOLECULAR THERAPY 27 (4), 322-323, 2019 | | 2019 |
High-Resolution Functional Dissection of Enhancers within the B-Globin Locus Control Region using a Lentiviral Vector-Based Massively Parallel Reporter Assay M Unti, F Ma, RP Hollis, DB Kohn, RA Morgan MOLECULAR THERAPY 27 (4), 417-417, 2019 | | 2019 |