| Patient-customized oligonucleotide therapy for a rare genetic disease J Kim, C Hu, C Moufawad El Achkar, LE Black, J Douville, A Larson, ... New England Journal of Medicine 381 (17), 1644-1652, 2019 | 527 | 2019 |
| Reversible conformational conversion of α-synuclein into toxic assemblies by glucosylceramide F Zunke, AC Moise, NR Belur, E Gelyana, I Stojkovska, H Dzaferbegovic, ... Neuron 97 (1), 92-107. e10, 2018 | 210 | 2018 |
| Stress-induced cellular clearance is mediated by the SNARE protein ykt6 and disrupted by α-Synuclein LK Cuddy, WY Wani, ML Morella, C Pitcairn, K Tsutsumi, K Fredriksen, ... Neuron 104 (5), 869-884. e11, 2019 | 62 | 2019 |
| Rescue of α-synuclein aggregation in Parkinson’s patient neurons by synergistic enhancement of ER proteostasis and protein trafficking I Stojkovska, WY Wani, F Zunke, NR Belur, EA Pavlenko, N Mwenda, ... Neuron 110 (3), 436-451. e11, 2022 | 58 | 2022 |
| Recombinant pro-CTSD (cathepsin D) enhances SNCA/α-synuclein degradation in α-synucleinopathy models S Prieto Huarcaya, A Drobny, ARA Marques, A Di Spiezio, JP Dobert, ... Autophagy 18 (5), 1127-1151, 2022 | 27 | 2022 |
| AAV9/MFSD8 gene therapy is effective in preclinical models of neuronal ceroid lipofuscinosis type 7 disease X Chen, T Dong, Y Hu, FC Shaffo, NR Belur, JR Mazzulli, SJ Gray The Journal of clinical investigation 132 (5), 2022 | 20 | 2022 |
| Pregnancy-Induced Amelioration of Muscular Dystrophy Phenotype in mdx Mice via Muscle Membrane Stabilization Effect of Glucocorticoid Y Shimizu-Motohashi, Y Asakura, N Motohashi, NR Belur, ... PLoS One 10 (3), e0120325, 2015 | 10 | 2015 |
| Preclinical results in rodents strongly support clinical evaluation of scAAV9/MFSD8 as a potential gene therapy for CLN7 patients X Chen, F Shaffo, T Dong, Y Hu, NR Belur, JR Mazzulli, SJ Gray Molecular Genetics and Metabolism 132 (2), S24, 2021 | 2 | 2021 |
| Nuclear aggregates of NONO/SFPQ and A-to-I-edited RNA in Parkinson’s disease and dementia with Lewy bodies NR Belur, BI Bustos, SJ Lubbe, JR Mazzulli Neuron, 2024 | | 2024 |
| Preclinical Results in Rodents Strongly Support Clinical Evaluation of scAAV9/MFSD8 as a Potential Gene Therapy for CLN7 Patients X Chen, F Shaffo, T Dong, Y Hu, N Belur, J Mazzulli, S Gray MOLECULAR THERAPY 28 (4), 563-563, 2020 | | 2020 |
| Preclinical efficacy and safety evaluation of scAAV9/CLN7 gene replacement therapy in rodents X Chen, F Shaffo, T Dong, Y Hu, NR Belur, JR Mazzulli, SJ Gray Molecular Genetics and Metabolism 129 (2), S40, 2020 | | 2020 |
| Direct reprogramming of fibroblasts into muscle or neural lineages by using single transcription factor with or without MyoD transactivation domain NR Belur University of Minnesota, 2014 | | 2014 |
| Stress-induced cellular clearance is mediated by SNARE protein ykt6 and disrupted by a-synuclein LK Cuddy, WY Wani, ML Morella, C Pitcairn, K Tsutsumi, K Fredriksen, ... | | |
