| Downregulation of microRNA-126 contributes to the failing right ventricle in pulmonary arterial hypertension F Potus, G Ruffenach, A Dahou, C Thebault, S Breuils-Bonnet, ... Circulation 132 (10), 932-943, 2015 | 210 | 2015 |
| A TRPA1 inhibitor suppresses neurogenic inflammation and airway contraction for asthma treatment A Balestrini, V Joseph, M Dourado, RM Reese, SD Shields, L Rougé, ... Journal of Experimental Medicine 218 (4), 2021 | 75 | 2021 |
| Human T cell generation is restored in CD3δ severe combined immunodeficiency through adenine base editing GE McAuley, G Yiu, PC Chang, GA Newby, B Campo-Fernandez, ... Cell 186 (7), 1398-1416. e23, 2023 | 36 | 2023 |
| Creating new β-globin-expressing lentiviral vectors by high-resolution mapping of locus control region enhancer sequences RA Morgan, F Ma, MJ Unti, D Brown, PG Ayoub, C Tam, L Lathrop, ... Molecular Therapy-Methods & Clinical Development 17, 999-1013, 2020 | 13 | 2020 |
| Lentiviral gene therapy for X-linked chronic granulomatous disease recapitulates endogenous CYBB regulation and expression RL Wong, S Sackey, D Brown, S Senadheera, K Masiuk, JP Quintos, ... Blood, The Journal of the American Society of Hematology 141 (9), 1007-1022, 2023 | 10 | 2023 |
| Bioinformatic-Guided Design of a Lentiviral Vector for X-Linked Chronic Granulomatous Diseases Recapitulates Endogenous CYBB Gene Regulation and Expression RL Wong, S Sackey, D Brown, K Masiuk, S Senadheera, JP Quintos, ... MOLECULAR THERAPY 30 (4), 386-386, 2022 | | 2022 |
| Bioinformatics-Guided Design of Endogenously Regulated Lentiviral Vectors for Hematopoietic Stem Cell Gene Therapy RL Wong UCLA, 2021 | | 2021 |
| Creating New b-Globin-Expressing Lentiviral Vectors by High-Resolution Mapping of Locus Control Region Enhancer Sequences RA Morgan, F Ma, MJ Unti, D Brown, PG Ayoub, C Tam, L Lathrop, ... | | |
