Organs to Cells and Cells to Organoids: The Evolution of in vitro Central Nervous System Modelling D Pacitti, R Privolizzi, BE Bax Frontiers in cellular neuroscience 13, 129, 2019 | 69 | 2019 |
A broad overview and review of CRISPR-Cas technology and stem cells SN Waddington, R Privolizzi, R Karda, HC O’Neill Current stem cell reports 2, 9-20, 2016 | 57 | 2016 |
Gene therapy restores dopamine transporter expression and ameliorates pathology in iPSC and mouse models of infantile parkinsonism J Ng, S Barral, C De La Fuente Barrigon, G Lignani, FA Erdem, ... Science translational medicine 13 (594), eaaw1564, 2021 | 25 | 2021 |
Viral gene therapy for paediatric neurological diseases: progress to clinical reality R Privolizzi, WS Chu, M Tijani, J Ng Developmental Medicine & Child Neurology 63 (9), 1019-1029, 2021 | 16 | 2021 |
The application of prophylactic antibodies for rhinovirus infections R Privolizzi, R Solari, SL Johnston, GR McLean Antiviral Chemistry and Chemotherapy 23 (5), 173-177, 2014 | 15 | 2014 |
Development of novel promoters for neurological gene therapy M Tijani, R Privolizzi, T Oosterveen, JM Iglesias, S Cooper, ... MOLECULAR THERAPY 27 (4), 262-262, 2019 | 2 | 2019 |
GENE THERAPY PREVENTS HEPATIC MITOCHONDRIAL DYSFUNCTION IN MURINE DEOXYGUANOSINE KINASE DEFICIENCY N Keshavan, M Greenwood, H Prunty, JF Antinao Diaz, R Privolizzi, ... bioRxiv, 2024.05. 10.593325, 2024 | | 2024 |
A High-Throughput AAV-Based Screening Platform for the Engineering of Cell-Type Specific Gene Regulatory Elements R Privolizzi, A Guijarro Belmar, P Demosthenous, H Luniak, CC Smith, ... Molecular Therapy 31 (4S1), 2023 | | 2023 |
A Human-Centric AAV Capsid Engineering Platform for the Targeting of Dysfunctional Neural Circuits A Guijarro Belmar, H Luniak, P Demosthenous, R Privolizzi, CC Smith, ... Molecular Therapy 31 (4S1), 2023 | | 2023 |
Engineering Ligand-Gated Ion Channels for Chemogenetic Modulation of Hyperexcitable Circuits in Neurological Disorders CC Smith, A Guijarro Belmar, H Luniak, P Demosthenous, R Privolizzi, ... Molecular Therapy 31 (4S1), 2023 | | 2023 |
In vivo evaluation of novel synthetic promoters for CNS gene therapy R Privolizzi, M Tijani, E Giardina, S Cooper, T Oosterveen, JM Iglesias, ... HUMAN GENE THERAPY 33 (23-24), A34-A35, 2022 | | 2022 |
Evaluation of a novel dopaminergic neuronal promoter design candidate in neonatal mice WS Chu, R Desai, R Privolizzi, R Karda, B Owusu-Yaw, SN Waddington, ... HUMAN GENE THERAPY 33 (23-24), A49-A49, 2022 | | 2022 |
Long term correction of Dopamine transporter deficiency syndrome following midbrain gene therapy J Ng, R Privolizzi, AA Rahim, MA Kurian, SN Waddington HUMAN GENE THERAPY 33 (23-24), A86-A86, 2022 | | 2022 |
In vivo evaluation of novel synthetic promoters for CNS gene therapy R Privolizzi University College London, 2022 | | 2022 |
In Vivo Evaluation of Novel Synthetic Promoters for CNS Gene Therapy R Privolizzi, M Tijani, E Giardina, S Cooper, T Oosterveen, JM Iglesias, ... HUMAN GENE THERAPY; Selected Oral Presentation at 28th ESGCT conference; 32 …, 2021 | | 2021 |
Gene therapy for Dopamine transporter deficiency syndrome: Infantile Parkinsonism-dystonia J Ng, S Barral, C Barrigon, G Lignani, F Erdem, R Wallings, R Privolizzi, ... HUMAN GENE THERAPY 32 (19-20), A50-A50, 2021 | | 2021 |
In Vivo Evaluation of Novel Synthetic Promoters for CNS Gene Therapy R Privolizzi, M Tijani, E Giardina, S Cooper, T Oosterveen, JM Iglesias, ... Molecular Therapy 29 (4S1), 283, 2021 | | 2021 |
Development of Novel Synthetic Promoters for CNS Gene Therapy R Privolizzi, M Tijani, E Giardina, S Cooper, T Oosterveen, JM Iglesias, ... MOLECULAR THERAPY 28 (4), 542-542, 2020 | | 2020 |
Development of novel synthetic promoters for CNS gene therapy R Privolizzi, M Tijani, T Oosterveen, E Giardina, JM Iglesias, S Cooper, ... HUMAN GENE THERAPY 30 (8), A12-A12, 2019 | | 2019 |
Gene Therapy for Infantile Parkinsonism J Ng, S Barral, CDLF Barrigon, G Lignani, FA Erdem, R Wallings, ... MOLECULAR THERAPY 27 (4), 257-257, 2019 | | 2019 |