| Hierarchical Bayesian modelling of disease progression to inform clinical trial design in centronuclear myopathy E Fouarge, A Monseur, B Boulanger, M Annoussamy, AM Seferian, ... Orphanet Journal of Rare Diseases 16, 1-11, 2021 | 22 | 2021 |
| Myostatin: a circulating biomarker correlating with disease in myotubular myopathy mice and patients C Koch, S Buono, A Menuet, A Robé, S Djeddi, C Kretz, R Gomez-Oca, ... Molecular Therapy Methods & Clinical Development 17, 1178-1189, 2020 | 15 | 2020 |
| Engrailed‐1 induces long‐lasting behavior benefit in an experimental Parkinson primate model N Thomasson, E Pioli, C Friedel, A Monseur, J Lavaur, KL Moya, ... Movement Disorders 34 (7), 1082-1084, 2019 | 14 | 2019 |
| Natural history study and statistical modeling of disease progression in a preclinical model of myotubular myopathy S Buono, A Monseur, A Menuet, A Robé, C Koch, J Laporte, L Thielemans, ... Disease Models & Mechanisms 15 (7), dmm049284, 2022 | 4 | 2022 |
| Leveraging natural history data in one-and two-arm hierarchical Bayesian studies of rare disease progression A Monseur, BP Carlin, B Boulanger, A Seferian, L Servais, C Freitag, ... Statistics in Biosciences, 1-22, 2022 | 1 | 2022 |
| Statistical modelling of disease progression in a preclinical model of myotubular myopathy S Buono, A Monseur, A Menuet, A Robe, C Koch, J Laporte, L Thielemans, ... NEUROMUSCULAR DISORDERS 31, S58-S58, 2021 | | 2021 |
| CONGENITAL MYOPATHIES–CENTRONUCLEAR MYOPATHIES: EP. 26 Leveraging natural history data in one-and two-arm hierarchical Bayesian studies of rare disease progression A Monseur, B Carlin, B Boulanger, A Seferian, L Servais, C Freitag, ... Neuromuscular Disorders 31, S57, 2021 | | 2021 |
| CONGENITAL MYOPATHIES–CENTRONUCLEAR MYOPATHIES: EP. 30 Statistical modelling of disease progression in a preclinical model of myotubular myopathy S Buono, A Monseur, A Menuet, A Robé, C Koch, J Laporte, L Thielemans, ... Neuromuscular Disorders 31, S58, 2021 | | 2021 |
| Computer Modeling Using Historical Data Demonstrates a Significant Reduction in Expected Extravascular Fibrinous Lesions Due to Congenital Plasminogen Deficiency While … JM Parker, D Craig, M Gaido, G Albert, A Monseur, AD Shapiro, J Moran Blood 130, 2371, 2017 | | 2017 |
| Myostatin: a Circulating Biomarker Correlating with Disease in Myotubular Myopathy Mice and Patients R Gomez-Oca, M Depla, A Monseur, L Thielemans, L Servais | | |
