| Cytosine and adenine base editing of the brain, liver, retina, heart and skeletal muscle of mice via adeno-associated viruses JM Levy, WH Yeh, N Pendse, JR Davis, E Hennessey, R Butcher, ... Nature biomedical engineering 4 (1), 97-110, 2020 | 353 | 2020 |
| In vivo assessment of potential therapeutic approaches for USH2A-associated diseases ND Pendse, V Lamas, BS Pawlyk, ML Maeder, ZY Chen, EA Pierce, Q Liu Retinal Degenerative Diseases: Mechanisms and Experimental Therapy, 91-96, 2019 | 31 | 2019 |
| Ift172 conditional knock-out mice exhibit rapid retinal degeneration and protein trafficking defects PR Gupta, N Pendse, SH Greenwald, M Leon, Q Liu, EA Pierce, ... Human molecular genetics 27 (11), 2012-2024, 2018 | 22 | 2018 |
| Deficiency of isoprenylcysteine carboxyl methyltransferase (ICMT) leads to progressive loss of photoreceptor function JR Christiansen, ND Pendse, S Kolandaivelu, MO Bergo, SG Young, ... Journal of Neuroscience 36 (18), 5107-5114, 2016 | 11 | 2016 |
| Exon 13-skipped USH2A protein retains functional integrity in mice, suggesting an exo-skipping therapeutic approach to treat USH2A-associated disease N Pendse, V Lamas, M Maeder, B Pawlyk, S Gloskowski, EA Pierce, ... BioRxiv, 2020.02. 04.934240, 2020 | 7 | 2020 |
| Efficient identification of therapeutic base editing candidates to correct human mutations in the USH2A gene Y Tachida, JM Levy, N Pendse, Q Liu, DR Liu, E Pierce, J Comander MOLECULAR THERAPY 28 (4), 324-324, 2020 | 1 | 2020 |
| CRISPR/Cas based evaluation of the therapeutic potential for USH2A associated diseases N Pendse, V Lamas, B Pawlyk, M Maeder, ZY Chen, E Pierce, Q Liu MOLECULAR THERAPY 27 (4), 317-318, 2019 | 1 | 2019 |
| An effective dimensional inspection method based on zone fitting NV Pendse Texas A&M University, 2006 | 1 | 2006 |
| Improving Gene Therapy Viral Vectors Via Capsid Engineering N Pendse American Society of Gene and Cell Therapy, 2022 | | 2022 |
| Targeted base editing of the ush2a gene DRLJMLHYCTAPQLN PENDSE US Patent WO2021222318A1, 2021 | | 2021 |
| CRISPR/Cas9-Mediated Exon-Skipping Approach for USH2A-Associated Usher Syndrome EA Pierce, CM Margulies, ND Pendse, SW Gloskowski, L Qin, ML Maeder US Patent App. 17/040,629, 2021 | | 2021 |
| Miniaturizing Usher Syndrome Type 2A Gene for Gene Therapy via Cell Proliferation W Wang, M Florea, N Pendse, Q Liu, L Vandenberghe MOLECULAR THERAPY 28 (4), 92-93, 2020 | | 2020 |
| Investigation of Base-Editing-Mediated Exon Skipping as a Potential Gene Therapy for Usher Syndrome RBQL Thuzar Thein, Nachiket Pendse Digital Access to Scholarship at Harvard, 19, 2020 | | 2020 |
| Development of a rapid and cost-effective CRISPR-based molecular detection platform for a novel myocilin mutation in rural Philippines. ER Collantes, N Pendse, A Dy, J Gootenberg, O Abudayyeh, B Fan, ... Investigative Ophthalmology & Visual Science 60 (9), 6076-6076, 2019 | | 2019 |
| Long-Term Rescue of Retinal Degeneration in Rho-P23H Knockin Mice via Dual AAV-Medicated Allele-Specific CRISPR-Cas9 Gene Editing A D'Amico, R Butcher, BP Kleinstiver, N Pendse, P Li, E Pierce, JK Joung, ... MOLECULAR THERAPY 27 (4), 430-430, 2019 | | 2019 |
| Evaluation of Therapeutic Potential of Human USH2A Gene Lacking Exon 13 (USH2A-Delta Ex13) for Restoring Ciliogenesis N Pendse, S Glowkowski, M Maeder, E Pierce, Q Liu MOLECULAR THERAPY 26 (5), 409-409, 2018 | | 2018 |
| Geranylgeranylation of retinal proteins is essential for cone photoreceptor function and survival ND Pendse, M Bergo, S Young, V Ramamurthy Investigative Ophthalmology & Visual Science 56 (7), 1322-1322, 2015 | | 2015 |
